Audentes Homepage 2017-11-30T12:11:13+00:00


Audentes Therapeutics is focused on developing and commercializing gene therapy products for patients suffering from serious, life-threatening rare diseases.

Courageous Patients

We believe patients, families and patient advocacy groups should have an integral role in all aspects of our drug development process, from the initiation of a clinical program to its completion and beyond.

Bold Effort

The science of making gene therapy products is complex. Our robust research laboratory and state-of-the-art vector manufacturing facility puts us at the forefront of developing gene therapy products. Our bold approach is driven by our commitment to bringing innovative treatments to patients living with serious, life-threatening rare genetic diseases as rapidly as possible.

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Our People

We take pride in our efforts to harness the transformative potential of AAV gene therapy to improve the lives of patients suffering from devastating rare diseases.


Media & Social Updates

Latest News


Audentes is different – we take time to understand our patient communities and weave that knowledge with our scientific insights to develop transformative therapies. Follow us on Facebook to share with us, stay updated and learn more.


What bold things can you expect from us next? Find out what events we’ll be participating in, plus keep track of company announcements, by following us on Twitter!

Learn more about what we’re doing to become the leader in the development and commercialization of innovative new gene therapy treatments, the people who make it great and the exciting job opportunities available by following us on LinkedIn.